Videos

Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping

Aurélie Goyenvalle¹, Arran Babbs¹, Dave Powell¹, Ryszard Kole², Sue Fletcher³, Steve D Wilton³ and Kay E Davies¹

¹MRC Functional Genomics Unit, Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford, UK; ²AVI Biopharma, Corvallis, Oregon, USA; ³Center for Neuromuscular and Neurological Disorders, University of Western Australia, Perth, Western Australia, Australia

Oct. 20, 3009; Molecular Therapy

Supplementary Video Links:

dKO Mouse No Treatment / Supplementary Video S1

dKO Mouse Post-Treatment with PPMO / Supplementary Video S2